Psychometric evaluation of the NTDT-PRO questionnaire for assessing symptoms in patients with non-transfusion-dependent beta-thalassaemia.

Ali T Taher Khaled M MusallamVip ViprakasitAntonis KattamisJennifer Lord-BessenAylin YucelShien GuoChristopher G PelligraAlan L ShieldsJeevan K ShettyDimana MitevaLuciana Moro BuenoMaria Domenica Cappellini

Published in: BMJ open (2023)

The NTDT-PRO demonstrated adequate psychometric properties to assess anaemia-related symptoms in adults with NTDT and can be used to evaluate treatment efficacy in clinical trials.

Keyphrases

psychometric properties
clinical trial
anti inflammatory
sleep quality
randomized controlled trial
cross sectional
sickle cell disease
physical activity
depressive symptoms
acute kidney injury
open label
iron deficiency
phase iii