Login / Signup

Muscle MRI as a biomarker of disease activity and progression in myotonic dystrophy type 1: a longitudinal study.

Laura FiondaLuca LeonardiLaura TufanoAntonio LaulettaStefania MorinoGioia MerlonghiRocco CostanzoElena RossiniFrancesca ForcinaDemetrio MarandoDavid Sarzi AmadèElisabetta BucciMarco SalvettiGiovanni AntoniniMatteo Garibaldi
Published in: Journal of neurology (2024)
Muscle MRI represents a sensitive biomarker of disease activity, severity, and progression in DM1. STIR alterations precede fat replacement and identify patients with a higher risk of disease progression, while T1-sequences reveal atrophy and fat replacement progression before clinical worsening.
Keyphrases