Factors Associated With Early Motor Function Trajectories in DMD After Glucocorticoid Initiation: Post Hoc Analysis of the FOR-DMD Trial.
Marianela SchiavaMichael P McDermottJonathan BroomfieldKeith R AbramsAnna G MayhewCraig M McDonaldWilliam B MartensStephanie J GregoryRobert C GriggsMichela Guglierinull nullPublished in: Neurology (2024)
Glucocorticoid regimen, age, duration of glucocorticoid exposure, and baseline COA performance need to be considered in the design and analysis of clinical trials in young boys with DMD.