Patient-reported, health economic and psychosocial outcomes in patients with Friedreich ataxia (PROFA): protocol of an observational study using momentary data assessments via mobile health app.
Maresa BuchholzNiklas WeberStephanie BorelSabrina SayahFeng XieJörg B SchulzKathrin ReetzSylvia BoeschThomas KlopstockIvan KarinLudger SchölsMarcus Grobe-EinslerThomas KlockgetherElin Haf DaviesMadeleine SchmederAndreas NadkeBernhard MichalowskyPublished in: BMJ open (2023)
ClinicalTrials.gov Registry (NCT05943002); Pre-results.