Safety of Sirolimus in Patients with Tuberous Sclerosis Complex under Two Years of Age-A Bicenter Retrospective Study.

Dominika Miszewska Sergiusz JozwiakKatarzyna Kotulska

Published in: Journal of clinical medicine (2023)

Adverse effects associated with sirolimus use in infants and young children with TSC are frequent yet not life- or health-threatening. Further multicenter prospective clinical trials should determine the long-term safety of sirolimus.

Keyphrases

clinical trial
healthcare
public health
mental health
cross sectional
randomized controlled trial
double blind
risk assessment
study protocol
climate change
phase iii