Longitudinal evaluation of SMN levels as biomarker for spinal muscular atrophy: results of a phase IIb double-blind study of salbutamol.

Danilo Francesco TizianoRosa LomastroEmanuela AbiusiMaria Barbara PasanisiLorena Di PietroStefania FioriGiovanni BaranelloCorrado AngeliniGianni SorarùAlessandra GaianiTiziana MonginiLiliana VercelliEugenio MercuriGessica VascoMarika PaneGiuseppe VitaGianluca VitaSonia MessinaRoberta PetilloLuigia PassamanoLuisa PolitanoAngela CampanellaRenato MantegazzaLucia Morandi

Published in: Journal of medical genetics (2018)

EudraCT no. 2007-001088-32.

Keyphrases

double blind
clinical trial
placebo controlled
cross sectional
randomized controlled trial
study protocol
phase ii