The effect of emicizumab prophylaxis on long-term, self-reported physical health in persons with haemophilia A without factor VIII inhibitors in the HAVEN 3 and HAVEN 4 studies.
Mark W SkinnerClaude NégrierIdo Paz-PrielSammy ChebonVictor Jimenez YusteMichael U CallaghanMichaela LehleMarkus NiggliJohnny N MahlanguAmy D ShapiroMidori ShimaAvrita Campinha-BacoteGallia G LevyJohannes OldenburgSylvia von MackensenSteven W PipePublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2021)
Emicizumab prophylaxis in PwHA without FVIII inhibitors resulted in persistent and meaningful improvements in Haem-A-QoL PH and less work disruption than previous treatment.