Stem cell transplantation for pediatric patients with adrenoleukodystrophy: A nationwide retrospective analysis in Japan.
Koji KatoHiromasa YabeNobuyuki ShimozawaSouichi AdachiMineo KurokawaYoshiko HashiiAtsushi SatoNao YoshidaMakiko KagaOsamu OnoderaShunichi KatoYoshiko AtsutaTomohiro MorioPublished in: Pediatric transplantation (2021)
Our study revealed that a reduced conditioning regimen with fludarabine/melphalan/low-dose TBI provides better outcomes, and the results of CBT significantly improved after 2007.