Access to innovative therapies in pediatric oncology: Report of the nationwide experience in Canada.
Sandra JuddGabriel Revon-RivièreStephanie A GroverRebecca J DeyellMagimairajan Issai VananVictor A LewisLucie PecheuxAlexandra P ZorziCatherine GoudieRaoul SantiagoThai Hoa TranLesleigh S AbbottJosee BrossardPaul MooreheadSaima AlviCarol PortwineAvram E DenburgJames A WhitlockSarah Cohen-GogoDaniel A MorgensternPublished in: Cancer medicine (2024)
This real-world data collection illustrates an increasing use of "out-of-trial" innovative therapies in pediatric oncology. This new field of practice warrants further studies to understand the impact on patient trajectory and equity in access to innovative therapies.