Long-term treatment of hereditary transthyretin amyloidosis with patisiran: multicentre, real-world experience in Italy.

Luca Gentile Anna Mazzeo Chiara Briani Silvia Casagrande Marcella De Luca Gian Maria Fabrizi Christian Gagliardi Chiara Gemelli Francesca Forcina Marina Grandis Valeria Guglielmino Giacomo Iabichella Luca Leonardi Alessandro Lozza Fiore Manganelli Roberta MussinelliFilomena MyGiuseppe Occhipinti Silvia Fenu Massimo Russo Angela Romano Alessandro Salvalaggio Matteo Tagliapietra Stefano Tozza Giovanni Palladini Laura Obici Marco Luigetti

Published in: Neurological sciences : official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology (2024)

Patisiran largely stabilised disease in patients with ATTRv amyloidosis.

Keyphrases

multiple myeloma
clinical trial
cross sectional
randomized controlled trial
replacement therapy