Aurelie T Goyenvalle (Aurelie Goyenvalle, Aurélie Goyenvalle, A Goyenvalle)

Publication Activity (10 Years)

Years Active: 2020-2024
Publications (10 Years): 32

Top Topics

Duchenne Muscular Dystrophy

Top Venues

Nucleic acid therapeutics

Proceedings of the National Academy of Sciences of the United States of America

This page only lists publications with an associated author ORCID identifier.

Publications

Mathilde Blitek, Xaysongkhame Phongsavanh, Aurelie T Goyenvalle
The bench to bedside journey of tricyclo-DNA antisense oligonucleotides for the treatment of Duchenne muscular dystrophy. RSC medicinal chemistry 15 (9) (2024)
Mathilde Doisy, Ophélie Vacca, Amel Saoudi, Aurelie T Goyenvalle
Levels of Exon-Skipping Are Not Artificially Overestimated Because of the Increased Affinity of Tricyclo-DNA-Modified Antisense Oligonucleotides to the Target DMD Exon. Nucleic acid therapeutics (2024)
Marika Faiella, Giada Botti, Alessandro Dalpiaz, Lorenzo Gnudi, Aurelie T Goyenvalle, Barbara Pavan, Daniela Perrone, Matteo Bovolenta, Elena Marchesi
In Vitro Studies to Evaluate the Intestinal Permeation of an Ursodeoxycholic Acid-Conjugated Oligonucleotide for Duchenne Muscular Dystrophy Treatment. Pharmaceutics 16 (8) (2024)
Marika Faiella, Giada Botti, Alessandro Dalpiaz, Lorenzo Gnudi, Aurelie T Goyenvalle, Barbara Pavan, Daniela Perrone, Matteo Bovolenta, Elena Marchesi
In Vitro Studies to Evaluate the Intestinal Permeation of an Ursodeoxycholic Acid-Conjugated Oligonucleotide for Duchenne Muscular Dystrophy Treatment. Pharmaceutics 16 (8) (2024)
Adrien Morin, Amalia Stantzou, Olga N Petrova, John C W Hildyard, Thomas Tensorer, Meriem Matouk, Mina V Petkova, Isabelle Richard, Tudor Manoliu, Aurelie T Goyenvalle, Sestina Falcone, Markus Schuelke, Corinne Laplace-Builhé, Richard J Piercy, Luis Garcia, Helge Amthor
Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America 120 (2) (2023)
Adrien Morin, Amalia Stantzou, Olga N Petrova, John C W Hildyard, Thomas Tensorer, Meriem Matouk, Mina V Petkova, Isabelle Richard, Tudor Manoliu, Aurelie T Goyenvalle, Sestina Falcone, Markus Schuelke, Corinne Laplace-Builhé, Richard J Piercy, Luis Garcia, Helge Amthor
Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America 120 (2) (2023)
Adrien Morin, Amalia Stantzou, Olga N Petrova, John C W Hildyard, Thomas Tensorer, Meriem Matouk, Mina V Petkova, Isabelle Richard, Tudor Manoliu, Aurelie T Goyenvalle, Sestina Falcone, Markus Schuelke, Corinne Laplace-Builhé, Richard J Piercy, Luis Garcia, Helge Amthor
Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America 120 (2) (2023)
Flavien Bizot, Thomas Tensorer, Luis Garcia, Aurelie T Goyenvalle
Impact of the Inhibition of Organic Anion Transporter on Tricyclo-DNA-Mediated Exon Skipping in the mdx Mouse Model. Nucleic acid therapeutics (2023)
Adrien Morin, Amalia Stantzou, Olga N Petrova, John C W Hildyard, Thomas Tensorer, Meriem Matouk, Mina V Petkova, Isabelle Richard, Tudor Manoliu, Aurelie T Goyenvalle, Sestina Falcone, Markus Schuelke, Corinne Laplace-Builhé, Richard J Piercy, Luis Garcia, Helge Amthor
Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America 120 (2) (2023)
Amel Saoudi, Claire Fergus, Talia E Gileadi, Federica Montanaro, Jennifer E Morgan, Vincent P Kelly, Thomas Tensorer, Luis Garcia, Cyrille Vaillend, Francesco Muntoni, Aurelie T Goyenvalle
Investigating the Impact of Delivery Routes for Exon Skipping Therapies in the CNS of DMD Mouse Models. Cells 12 (6) (2023)
Mathilde Doisy, Ophélie Vacca, Claire Fergus, Talia Gileadi, Minou Verhaeg, Amel Saoudi, Thomas Tensorer, Luis Garcia, Vincent P Kelly, Federica Montanaro, Jennifer E Morgan, Maaike van Putten, Annemieke M Aartsma-Rus, Cyrille Vaillend, Francesco Muntoni, Aurelie T Goyenvalle
Networking to Optimize Dmd exon 53 Skipping in the Brain of mdx52 Mouse Model. Biomedicines 11 (12) (2023)
Mathilde Doisy, Ophélie Vacca, Claire Fergus, Talia Gileadi, Minou Verhaeg, Amel Saoudi, Thomas Tensorer, Luis Garcia, Vincent P Kelly, Federica Montanaro, Jennifer E Morgan, Maaike van Putten, Annemieke M Aartsma-Rus, Cyrille Vaillend, Francesco Muntoni, Aurelie T Goyenvalle
Networking to Optimize Dmd exon 53 Skipping in the Brain of mdx52 Mouse Model. Biomedicines 11 (12) (2023)
Flavien Bizot, Abdallah Fayssoil, Cécile Gastaldi, Tabitha Irawan, Xaysongkhame Phongsavanh, Arnaud Mansart, Thomas Tensorer, Elise Brisebard, Luis Garcia, Rudolph L Juliano, Aurelie T Goyenvalle
Oligonucleotide Enhancing Compound Increases Tricyclo-DNA Mediated Exon-Skipping Efficacy in the Mdx Mouse Model. Cells 12 (5) (2023)
Adrien Morin, Amalia Stantzou, Olga N Petrova, John C W Hildyard, Thomas Tensorer, Meriem Matouk, Mina V Petkova, Isabelle Richard, Tudor Manoliu, Aurelie T Goyenvalle, Sestina Falcone, Markus Schuelke, Corinne Laplace-Builhé, Richard J Piercy, Luis Garcia, Helge Amthor
Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America 120 (2) (2023)
Amel Saoudi, Claire Fergus, Talia E Gileadi, Federica Montanaro, Jennifer E Morgan, Vincent P Kelly, Thomas Tensorer, Luis Garcia, Cyrille Vaillend, Francesco Muntoni, Aurelie T Goyenvalle
Investigating the Impact of Delivery Routes for Exon Skipping Therapies in the CNS of DMD Mouse Models. Cells 12 (6) (2023)
Amel Saoudi, Claire Fergus, Talia E Gileadi, Federica Montanaro, Jennifer E Morgan, Vincent P Kelly, Thomas Tensorer, Luis Garcia, Cyrille Vaillend, Francesco Muntoni, Aurelie T Goyenvalle
Investigating the Impact of Delivery Routes for Exon Skipping Therapies in the CNS of DMD Mouse Models. Cells 12 (6) (2023)
Flavien Bizot, Abdallah Fayssoil, Cécile Gastaldi, Tabitha Irawan, Xaysongkhame Phongsavanh, Arnaud Mansart, Thomas Tensorer, Elise Brisebard, Luis Garcia, Rudolph L Juliano, Aurelie T Goyenvalle
Oligonucleotide Enhancing Compound Increases Tricyclo-DNA Mediated Exon-Skipping Efficacy in the Mdx Mouse Model. Cells 12 (5) (2023)
Flavien Bizot, Abdallah Fayssoil, Cécile Gastaldi, Tabitha Irawan, Xaysongkhame Phongsavanh, Arnaud Mansart, Thomas Tensorer, Elise Brisebard, Luis Garcia, Rudolph L Juliano, Aurelie T Goyenvalle
Oligonucleotide Enhancing Compound Increases Tricyclo-DNA Mediated Exon-Skipping Efficacy in the Mdx Mouse Model. Cells 12 (5) (2023)
Aurelie T Goyenvalle, Cecilia Jimenez-Mallebrera, Willeke M C van Roon-Mom, Sabine Sewing, Arthur M Krieg, Virginia Arechavala-Gomeza, Patrik Andersson
Considerations in the Preclinical Assessment of the Safety of Antisense Oligonucleotides. Nucleic acid therapeutics 33 (1) (2022)
Faouzi Zarrouki, Karima Relizani, Flavien Bizot, Thomas Tensorer, Luis Garcia, Cyrille Vaillend, Aurelie T Goyenvalle
Partial Restoration of Brain Dystrophin and Behavioral Deficits by Exon Skipping in the Muscular Dystrophy X-Linked (mdx) Mouse. Annals of neurology 92 (2) (2022)
Aurelie T Goyenvalle, Cecilia Jimenez-Mallebrera, Willeke M C van Roon-Mom, Sabine Sewing, Arthur M Krieg, Virginia Arechavala-Gomeza, Patrik Andersson
Considerations in the Preclinical Assessment of the Safety of Antisense Oligonucleotides. Nucleic acid therapeutics 33 (1) (2022)
Aurelie T Goyenvalle, Cecilia Jimenez-Mallebrera, Willeke M C van Roon-Mom, Sabine Sewing, Arthur M Krieg, Virginia Arechavala-Gomeza, Patrik Andersson
Considerations in the Preclinical Assessment of the Safety of Antisense Oligonucleotides. Nucleic acid therapeutics 33 (1) (2022)
Aurelie T Goyenvalle, Cecilia Jimenez-Mallebrera, Willeke M C van Roon-Mom, Sabine Sewing, Arthur M Krieg, Virginia Arechavala-Gomeza, Patrik Andersson
Considerations in the Preclinical Assessment of the Safety of Antisense Oligonucleotides. Nucleic acid therapeutics 33 (1) (2022)
Aurelie T Goyenvalle, Cecilia Jimenez-Mallebrera, Willeke M C van Roon-Mom, Sabine Sewing, Arthur M Krieg, Virginia Arechavala-Gomeza, Patrik Andersson
Considerations in the Preclinical Assessment of the Safety of Antisense Oligonucleotides. Nucleic acid therapeutics (2022)
Aurelie T Goyenvalle, Cecilia Jimenez-Mallebrera, Willeke M C van Roon-Mom, Sabine Sewing, Arthur M Krieg, Virginia Arechavala-Gomeza, Patrik Andersson
Considerations in the Preclinical Assessment of the Safety of Antisense Oligonucleotides. Nucleic acid therapeutics 33 (1) (2022)
Faouzi Zarrouki, Sébastien Goutal, Ophélie Vacca, Luis Garcia, Nicolas Tournier, Aurelie T Goyenvalle, Cyrille Vaillend
Abnormal Expression of Synaptic and Extrasynaptic GABA A Receptor Subunits in the Dystrophin-Deficient mdx Mouse. International journal of molecular sciences 23 (20) (2022)
Flavien Bizot, Adeline Vulin, Aurelie T Goyenvalle
Current Status of Antisense Oligonucleotide-Based Therapy in Neuromuscular Disorders. Drugs 80 (14) (2021)
Suzan M Hammond, Annemieke M Aartsma-Rus, Sandra Alves, Sven Even F Borgos, Ronald A M Buijsen, Rob W J Collin, Giuseppina Covello, Michela Alessandra Denti, Lourdes Ruiz Desviat, Lucía Echevarría, Camilla Foged, Gisela Gaina, Alejandro Garanto, Aurelie T Goyenvalle, Magdalena Guzowska, Irina Kholodnyuk, David R Jones, Sabine Krause, Taavi Lehto, Marisol Montolio, Willeke M C van Roon-Mom, Virginia Arechavala-Gomeza
Delivery of oligonucleotide-based therapeutics: challenges and opportunities. EMBO molecular medicine 13 (4) (2021)
Amel Saoudi, Aurelie T Goyenvalle
[RNA splicing modulation: Therapeutic progress and perspectives]. Medecine sciences : M/S 37 (6-7) (2021)
Karima Relizani, Lucía Echevarría, Faouzi Zarrouki, Cécile Gastaldi, Chloe Dambrune, Philippine Aupy, Adrian Haeberli, Marek Komisarski, Thomas Tensorer, Thibaut Larcher, Fedor Svinartchouk, Cyrille Vaillend, Luis Garcia, Aurelie T Goyenvalle
Palmitic acid conjugation enhances potency of tricyclo-DNA splice switching oligonucleotides. Nucleic acids research (2021)
M V Petkova, Amalia Stantzou, Adrien Morin, O Petrova, S Morales-Gonzalez, F Seifert, J Bellec-Dyevre, Tudor Manoliu, Aurelie T Goyenvalle, L Garcia, Isabelle Richard, Corinne Laplace-Builhé, Markus Schuelke, Helge Amthor
Live-imaging of revertant and therapeutically restored dystrophin in the DmdEGFP-mdx mouse model for Duchenne muscular dystrophy. Neuropathology and applied neurobiology 46 (6) (2020)
Simon A Krooss, Sonja Werwitzke, Johannes Kopp, Alice Rovai, Dirk Varnholt, Amelie S Wachs, Aurelie T Goyenvalle, Annemieke M Aartsma-Rus, Michael Ott, Andreas Tiede, Jörg Langemeier, Jens Bohne
Pathological mechanism and antisense oligonucleotide-mediated rescue of a non-coding variant suppressing factor 9 RNA biogenesis leading to hemophilia B. PLoS genetics 16 (4) (2020)