Efrain Sanchez-Ortiz (E Sanchez-Ortiz, Efrain Sánchez-Ortiz)

Publication Activity (10 Years)

Years Active: 2017-2022
Publications (10 Years): 6

Top Topics

Klebsiella Pneumoniae

Top Venues

Science advances

Science (New York, N.Y.)

Science translational medicine

This page only lists publications with an associated author ORCID identifier.

Publications

Takahiko Nishiyama, Yu Zhang, Miao Cui, Hui Li, Efrain Sanchez-Ortiz, John R McAnally, Wei Tan, Jiwoong Kim, Kenian Chen, Lin Xu, Rhonda Bassel-Duby, Eric N Olson
Precise genomic editing of pathogenic mutations in RBM20 rescues dilated cardiomyopathy. Science translational medicine 14 (672) (2022)
Francesco Chemello, Andreas C Chai, Hui Li, Cristina Rodriguez-Caycedo, Efrain Sanchez-Ortiz, Ayhan Atmanli, Alex A Mireault, Ning Liu, Rhonda Bassel-Duby, Eric N Olson
Precise correction of Duchenne muscular dystrophy exon deletion mutations by base and prime editing. Science advances 7 (18) (2021)
Yu Zhang, Hui Li, Yi-Li Min, Efrain Sanchez-Ortiz, Jian Huang, Alex A Mireault, John M Shelton, Jiwoong Kim, Pradeep P A Mammen, Rhonda Bassel-Duby, Eric N Olson
Enhanced CRISPR-Cas9 correction of Duchenne muscular dystrophy in mice by a self-complementary AAV delivery system. Science advances 6 (8) (2020)
Leonela Amoasii, John C W Hildyard, Hui Li, Efrain Sanchez-Ortiz, Alex A Mireault, Daniel Caballero, Rachel C M Harron, Thaleia-Rengina Stathopoulou, Claire Massey, John M Shelton, Rhonda Bassel-Duby, Richard J Piercy, Eric N Olson
Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy. Science (New York, N.Y.) 362 (6410) (2018)
Leonela Amoasii, Chengzu Long, Hui Li, Alex A Mireault, John M Shelton, Efrain Sanchez-Ortiz, John R McAnally, Samadrita Bhattacharyya, Florian Schmidt, Dirk Grimm, Stephen D Hauschka, Rhonda Bassel-Duby, Eric N Olson
Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy. Science translational medicine 9 (418) (2018)
Pengpeng Bi, Andres Ramirez-Martinez, Hui Li, Jessica Cannavino, John R McAnally, John M Shelton, Efrain Sanchez-Ortiz, Rhonda Bassel-Duby, Eric N Olson
Control of muscle formation by the fusogenic micropeptide myomixer. Science (New York, N.Y.) 356 (6335) (2017)