Federico Mingozzi

Publication Activity (10 Years)

Years Active: 2020-2022
Publications (10 Years): 9

Top Topics

Vascular Endothelial Growth Factor

Top Venues

Science advances

Liver international : official journal of the International Association for the Study of the Liver

Nature medicine

This page only lists publications with an associated author ORCID identifier.

Publications

Sem J Aronson, Norman Junge, Mediha Trabelsi, Wided Kelmemi, Aurelie Hubert, Karlla W Brigatti, Michael D Fox, Robert J de Knegt, Johanna C Escher, Virginia M Ginocchio, Raffaele Iorio, Yan Zhu, Figen Özçay, Fakher Rahim, Mortada H F El-Shabrawi, Eyal Shteyer, Angelo Di Giorgio, Lorenzo D'Antiga, Federico Mingozzi, Nicola Brunetti-Pierri, Kevin A Strauss, Philippe Labrune, Ridha Mrad, Ulrich Baumann, Ulrich H W Beuers, Piter J Bosma, null null
Disease burden and management of Crigler-Najjar syndrome: Report of a world registry. Liver international : official journal of the International Association for the Study of the Liver 42 (7) (2022)
Jihad El Andari, Edith Renaud-Gabardos, Warut Tulalamba, Jonas Weinmann, Louise Mangin, Quang Hong Pham, Susanne Hille, Antonette Bennett, Esther Attebi, Emanuele Bourges, Christian Leborgne, Nicolas Guerchet, Julia Fakhiri, Chiara Krämer, Ellen Wiedtke, Robert McKenna, Laurence Guianvarc'h, Magali Toueille, Giuseppe Ronzitti, Matthias Hebben, Federico Mingozzi, Thierry VandenDriessche, Mavis Agbandje-McKenna, Oliver J Müller, Marinee K Chuah, Ana Buj-Bello, Dirk Grimm
Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders. Science advances 8 (38) (2022)
Helena Costa-Verdera, Fanny Collaud, Christopher R Riling, Pauline Sellier, Jayme M L Nordin, G Michael Preston, Umut Cagin, Julien Fabregue, Simon Barral, Maryse Moya-Nilges, Jacomina Krijnse-Locker, Laetitia van Wittenberghe, Natalie Daniele, Bernard Gjata, Jeremie Cosette, Catalina Abad, Marcelo Simon-Sola, Severine Charles, Mathew Li, Marco Crosariol, Tom Antrilli, William J Quinn, David A Gross, Olivier Boyer, Xavier M Anguela, Sean M Armour, Pasqualina Colella, Giuseppe Ronzitti, Federico Mingozzi
Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates. Nature communications 12 (1) (2021)
Paul E Monahan, Claude Négrier, Michael Tarantino, Leonard A Valentino, Federico Mingozzi
Emerging Immunogenicity and Genotoxicity Considerations of Adeno-Associated Virus Vector Gene Therapy for Hemophilia. Journal of clinical medicine 10 (11) (2021)
Volha V Zhukouskaya, Louisa Jauze, Séverine Charles, Christian Leborgne, Stéphane Hilliquin, Jérémy Sadoine, Lotfi Slimani, Brigitte Baroukh, Laetitia van Wittenberghe, Nathalie Daniele, Fabienne Rajas, Agnès Linglart, Federico Mingozzi, Catherine Chaussain, Claire Bardet, Giuseppe Ronzitti
A novel therapeutic strategy for skeletal disorders: Proof of concept of gene therapy for X-linked hypophosphatemia. Science advances 7 (44) (2021)
Elena Barbon, Charlotte Kawecki, Solenne Marmier, Aboud Sakkal, Fanny Collaud, Severine Charles, Giuseppe Ronzitti, Caterina Casari, Olivier D Christophe, Cecile V Denis, Peter J Lenting, Federico Mingozzi
Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor. Gene therapy (2021)
Ying Kai Chan, Sean K Wang, Colin J Chu, David A Copland, Alexander J Letizia, Helena Costa-Verdera, Jessica J Chiang, Meher Sethi, May K Wang, William J Neidermyer, Yingleong Chan, Elaine T Lim, Amanda R Graveline, Melinda Sanchez, Ryan F Boyd, Thomas S Vihtelic, Rolando Gian Carlo O Inciong, Jared M Slain, Priscilla J Alphonse, Yunlu Xue, Lindsey R Robinson-McCarthy, Jenny M Tam, Maha H Jabbar, Bhubanananda Sahu, Janelle F Adeniran, Manish Muhuri, Phillip W L Tai, Jun Xie, Tyler B Krause, Andyna Vernet, Matthew Pezone, Ru Xiao, Tina Liu, Wei Wang, Henry J Kaplan, Guangping Gao, Andrew D Dick, Federico Mingozzi, Maureen A McCall, Constance L Cepko, George M Church
Engineering adeno-associated viral vectors to evade innate immune and inflammatory responses. Science translational medicine 13 (580) (2021)
Elena Barbon, Gabriel Ayme, Amel Mohamadi, Jean-François Ottavi, Charlotte Kawecki, Caterina Casari, Sebastien Verhenne, Solenne Marmier, Laetitia van Wittenberghe, Severine Charles, Fanny Collaud, Cecile V Denis, Olivier D Christophe, Federico Mingozzi, Peter J Lenting
Single-domain antibodies targeting antithrombin reduce bleeding in hemophilic mice with or without inhibitors. EMBO molecular medicine 12 (4) (2020)
Christian Leborgne, Elena Barbon, Jeffrey M Alexander, Hayley Hanby, Sandrine Delignat, Daniel M Cohen, Fanny Collaud, Saghana Muraleetharan, Dan Lupo, Joseph Silverberg, Karen Huang, Laetitia van Wittengerghe, Béatrice Marolleau, Adeline Miranda, Anna Fabiano, Victoria Daventure, Heena Beck, Xavier M Anguela, Giuseppe Ronzitti, Sean M Armour, Sébastien Lacroix-Desmazes, Federico Mingozzi
IgG-cleaving endopeptidase enables in vivo gene therapy in the presence of anti-AAV neutralizing antibodies. Nature medicine 26 (7) (2020)