Novel approaches for HTLV-1 therapy: innovative applications of CRISPR-Cas9.
Wilson DominguesVictor Ângelo FolgosiSabri Saeed SanabaniPedro Domingos Leite JuniorTatiane AssoneJorge Simão do Rosário CassebPublished in: Revista do Instituto de Medicina Tropical de Sao Paulo (2024)
The human T-cell lymphotropic virus type 1 (HTLV-1) is a single-stranded positive-sense RNA virus that belongs to the Retroviridae family, genus Deltaretro, and infects approximately five to 10 million people worldwide. Although a significant number of individuals living with HTLV-1 remain asymptomatic throughout their lives, some develop one or more severe clinical conditions, such as HTLV-1-associated myelopathy/tropical spastic paraparesis (HAM/TSP), a progressive and debilitating disease, and/or a subtype of non-Hodgkin's lymphoma with a more threatening course known as adult T-cell leukemia/lymphoma (ATLL). Moreover, current therapeutic options are limited and focus primarily on treating symptoms and controlling viral latency. CRISPR-Cas9 gene editing is proposed as a promising tool to address the intricate links associated with HTLV-1. By targeting or silencing key genes during initial infection and dysregulating immune signaling pathways, CRISPR-Cas9 offers potential intervention opportunities. In this review, we address the therapeutic potential of CRISPR-Cas9 gene editing, as well as examine the primary mechanisms involved in editing potential target genes and discuss the existing evidence in the current scientific literature.
Keyphrases
- crispr cas
- genome editing
- diffuse large b cell lymphoma
- genome wide
- endothelial cells
- randomized controlled trial
- signaling pathway
- multiple sclerosis
- spinal cord
- systematic review
- acute myeloid leukemia
- bone marrow
- stem cells
- genome wide identification
- risk assessment
- gene expression
- mesenchymal stem cells
- human health
- oxidative stress
- transcription factor
- nucleic acid
- bioinformatics analysis
- pluripotent stem cells
- disease virus